This issue of Hematology/Oncology Clinics, edited by Dr. Ali Taher, focuses on Thalassemia. Topics include, but are not limited to, Molecular basis and genetic modifiers; Evolving spectrum of epidemiology; Clinical classification; Ineffective erythropoiesis, anemia and iron overload; Hypercoagulability and vascular disease; Clinical complications and their management; Transfusion and iron chelation therapy; Hematopoietic Stem Cell Transplantation in Thalassemia; Gene therapy and genome editing; Emerging therapies; Quality of life; Advances in understanding pathophysiology and treatment of fertility, pregnancy, and prenatal diagnosis in Thalassemia; and MRI for iron overload.
Author Information
By Ali Taher, MD, PhD, FRCP, Professor of Medicine, Hematology & Oncology
Director – Fellowship and Residents Research Program, Faculty of Medicine
Associate Chair – Research, Department of Internal Medicine
Deputy Director – Naef K. Basile Cancer Institute
American University of Beirut Medical Center
Beirut – Lebanon
Professor of Hematology & Medical Oncology (Adj.)
Emory School of Medicine
Atlanta – USA
Thalassemia – Table of Contents
Erratum
Preface: Thalassemia
The Evolving Spectrum of the Epidemiology of Thalassemia
Molecular Basis and Genetic Modifiers of Thalassemia
Clinical Classification, Screening, and Diagnosis for Thalassemia
Ineffective Erythropoiesis: Anemia and Iron Overload
Clinical Complications and Their Management
Hypercoagulability and Vascular Disease
Interaction of Transfusion and Iron Chelation in Thalassemias
Iron Chelation Therapy as a Modality of Management
MRI for Iron Overload in Thalassemia
Fertility and Pregnancy in Women with Transfusion-Dependent Thalassemia
Hematopoietic Stem Cell Transplantation in Thalassemia
Gene Therapy and Genome Editing
Emerging Therapies